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Efficacy of exon-skipping therapy for DMD cardiomyopathy with mutations in actin binding domain 1 |
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Titel: |
Efficacy of exon-skipping therapy for DMD cardiomyopathy with mutations in actin binding domain 1 |
Auteur: |
Shiba, Naoko Yang, Xiao Sato, Mitsuto Kadota, Shin Suzuki, Yota Agata, Masahiro Nagamine, Kohei Izumi, Masaki Honda, Yusuke Koganehira, Tomoya Kobayashi, Hideki Ichimura, Hajime Chuma, Shinichiro Nakai, Junichi Tohyama, Shugo Fukuda, Keiichi Miyazaki, Daigo Nakamura, Akinori Shiba, Yuji |
Verschenen in: |
Molecular therapy - nucleic acids |
Paginering: |
Jaargang 34 () nr. C pagina's p. |
Jaar: |
2023 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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