Specific DMPK-promoter targeting by CRISPRi reverses myotonic dystrophy type 1-associated defects in patient muscle cells
Title:
Specific DMPK-promoter targeting by CRISPRi reverses myotonic dystrophy type 1-associated defects in patient muscle cells
Author:
Porquet, Florent Weidong, Lin Jehasse, Kévin Gazon, Hélène Kondili, Maria Blacher, Silvia Massotte, Laurent Di Valentin, Emmannuel Furling, Denis Gillet, Nicolas Albert Klein, Arnaud François Seutin, Vincent Willems, Luc