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Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies |
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Titel: |
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies |
Auteur: |
Brusson, Mégane Chalumeau, Anne Martinucci, Pierre Romano, Oriana Felix, Tristan Poletti, Valentina Scaramuzza, Samantha Ramadier, Sophie Masson, Cecile Ferrari, Giuliana Mavilio, Fulvio Cavazzana, Marina Amendola, Mario Miccio, Annarita |
Verschenen in: |
Molecular therapy - nucleic acids |
Paginering: |
Jaargang 32 () nr. C pagina's 229-246 |
Jaar: |
2023 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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