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Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies |
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Titel: |
Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies |
Auteur: |
Venkatesan, Vigneshwaran Christopher, Abisha Crystal Rhiel, Manuel Azhagiri, Manoj Kumar K. Babu, Prathibha Walavalkar, Kaivalya Saravanan, Bharath Andrieux, Geoffroy Rangaraj, Sumathi Srinivasan, Saranya Karuppusamy, Karthik V. Jacob, Annlin Bagchi, Abhirup Pai, Aswin Anand Nakamura, Yukio Kurita, Ryo Balasubramanian, Poonkuzhali Pai, Rekha Marepally, Srujan Kumar Mohankumar, Kumarasamypet Murugesan Velayudhan, Shaji R. Boerries, Melanie Notani, Dimple Cathomen, Toni Srivastava, Alok Thangavel, Saravanabhavan |
Verschenen in: |
Molecular therapy - nucleic acids |
Paginering: |
Jaargang 32 () nr. C pagina's 671-688 |
Jaar: |
2023 |
Inhoud: |
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Uitgever: |
The Author(s) |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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