Subretinal gene therapy delays vision loss in a Bardet-Biedl Syndrome type 10 mouse model
Titel:
Subretinal gene therapy delays vision loss in a Bardet-Biedl Syndrome type 10 mouse model
Auteur:
Hsu, Ying Bhattarai, Sajag Thompson, Jacob M. Mahoney, Angela Thomas, Jacintha Mayer, Sara K. Datta, Poppy Garrison, Janelle Searby, Charles C. Vandenberghe, Luk H. Seo, Seongjin Sheffield, Val C. Drack, Arlene V.