Correlating In Vitro Splice Switching Activity With Systemic In Vivo Delivery Using Novel ZEN-modified Oligonucleotides
Titel:
Correlating In Vitro Splice Switching Activity With Systemic In Vivo Delivery Using Novel ZEN-modified Oligonucleotides
Auteur:
Hammond, Suzan M McClorey, Graham Nordin, Joel Z Godfrey, Caroline Stenler, Sofia Lennox, Kim A Smith, CI Edvard Jacobi, Ashley M Varela, Miguel A Lee, Yi Behlke, Mark A Wood, Matthew J A Andaloussi, Samir E L