Antisense Oligonucleotide-mediated Suppression of Muscle Glycogen Synthase 1 Synthesis as an Approach for Substrate Reduction Therapy of Pompe Disease
Titel:
Antisense Oligonucleotide-mediated Suppression of Muscle Glycogen Synthase 1 Synthesis as an Approach for Substrate Reduction Therapy of Pompe Disease
Auteur:
Clayton, Nicholas P Nelson, Carol A Weeden, Timothy Taylor, Kristin M Moreland, Rodney J Scheule, Ronald K Phillips, Lucy Leger, Andrew J Cheng, Seng H Wentworth, Bruce M