Exon skipping induces uniform dystrophin rescue with dose-dependent restoration of serum miRNA biomarkers and muscle biophysical properties
Titel:
Exon skipping induces uniform dystrophin rescue with dose-dependent restoration of serum miRNA biomarkers and muscle biophysical properties
Auteur:
Chwalenia, Katarzyna Oieni, Jacopo Zemła, Joanna Lekka, Małgorzata Ahlskog, Nina Coenen-Stass, Anna M.L. McClorey, Graham Wood, Matthew J.A. Lomonosova, Yulia Roberts, Thomas C.