Developing antisense oligonucleotides for a TECPR2 mutation-induced, ultra-rare neurological disorder using patient-derived cellular models
Titel:
Developing antisense oligonucleotides for a TECPR2 mutation-induced, ultra-rare neurological disorder using patient-derived cellular models
Auteur:
Williams, Luis A. Gerber, David J. Elder, Amy Tseng, Wei Chou Baru, Valeriya Delaney-Busch, Nathaniel Ambrosi, Christina Mahimkar, Gauri Joshi, Vaibhav Shah, Himali Harikrishnan, Karthiayani Upadhyay, Hansini Rajendran, Sakthi H. Dhandapani, Aishwarya Meier, Joshua Ryan, Steven J. Lewarch, Caitlin Black, Lauren Douville, Julie Cinquino, Stefania Legakis, Helen Nalbach, Karsten Behrends, Christian Sato, Ai Galluzzi, Lorenzo Yu, Timothy W. Brown, Duncan Agrawal, Sudhir Margulies, David Kopin, Alan Dempsey, Graham T.