mRNA-based therapy in a rabbit model of variegate porphyria offers new insights into the pathogenesis of acute attacks
Titel:
mRNA-based therapy in a rabbit model of variegate porphyria offers new insights into the pathogenesis of acute attacks
Auteur:
Jericó, Daniel Córdoba, Karol M. Jiang, Lei Schmitt, Caroline Morán, María Sampedro, Ana Alegre, Manuel Collantes, María Santamaría, Eva Alegre, Estíbaliz Culerier, Corinne de Mendoza, Ander Estella-Hermoso Oyarzabal, Julen Martín, Miguel A. Peñuelas, Iván Ávila, Matías A. Gouya, Laurent Martini, Paolo G.V. Fontanellas, Antonio