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Selective suppression of polyglutamine-expanded protein by lipid nanoparticle-delivered siRNA targeting CAG expansions in the mouse CNS |
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Titel: |
Selective suppression of polyglutamine-expanded protein by lipid nanoparticle-delivered siRNA targeting CAG expansions in the mouse CNS |
Auteur: |
Hirunagi, Tomoki Sahashi, Kentaro Tachikawa, Kiyoshi Leu, Angel I. Nguyen, Michelle Mukthavaram, Rajesh Karmali, Priya P. Chivukula, Padmanabh Tohnai, Genki Iida, Madoka Onodera, Kazunari Ohyama, Manabu Okada, Yohei Okano, Hideyuki Katsuno, Masahisa |
Verschenen in: |
Molecular therapy - nucleic acids |
Paginering: |
Jaargang 24 () nr. C pagina's 1-10 |
Jaar: |
2021 |
Inhoud: |
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Uitgever: |
The Author(s) |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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