Targeting the 5′ untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy
Titel:
Targeting the 5′ untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy
Auteur:
Winkelsas, Audrey M. Grunseich, Christopher Harmison, George G. Chwalenia, Katarzyna Rinaldi, Carlo Hammond, Suzan M. Johnson, Kory Bowerman, Melissa Arya, Sukrat Talbot, Kevin Wood, Matthew J. Fischbeck, Kenneth H.