Mutant Allele-Specific CRISPR Disruption in DYT1 Dystonia Fibroblasts Restores Cell Function
Titel:
Mutant Allele-Specific CRISPR Disruption in DYT1 Dystonia Fibroblasts Restores Cell Function
Auteur:
Cruz, Lilian György, Bence Cheah, Pike See Kleinstiver, Benjamin P. Eimer, William A. Garcia, Sara P. Sharma, Nutan Ozelius, Laurie J. Bragg, D. Cristopher Joung, J. Keith Norberto de Souza, Osmar Macedo Timmers, Luis Fernando Saraiva Breakefield, Xandra O.