Antisense Oligonucleotide- and CRISPR-Cas9-Mediated Rescue of mRNA Splicing for a Deep Intronic CLRN1 Mutation
Titel:
Antisense Oligonucleotide- and CRISPR-Cas9-Mediated Rescue of mRNA Splicing for a Deep Intronic CLRN1 Mutation
Auteur:
Panagiotopoulos, Anna-Lena Karguth, Nina Pavlou, Marina Böhm, Sybille Gasparoni, Gilles Walter, Jörn Graf, Alexander Blum, Helmut Biel, Martin Riedmayr, Lisa Maria Becirovic, Elvir