Suppression of Mutant Protein Expression in SCA3 and SCA1 Mice Using a CAG Repeat-Targeting Antisense Oligonucleotide
Titel:
Suppression of Mutant Protein Expression in SCA3 and SCA1 Mice Using a CAG Repeat-Targeting Antisense Oligonucleotide
Auteur:
Kourkouta, Eleni Weij, Rudie González-Barriga, Anchel Mulder, Melissa Verheul, Ruurd Bosgra, Sieto Groenendaal, Bas Puoliväli, Jukka Toivanen, Jussi van Deutekom, Judith C.T. Datson, Nicole A.