Targeting RNA-Mediated Toxicity in C9orf72 ALS and/or FTD by RNAi-Based Gene Therapy
Titel:
Targeting RNA-Mediated Toxicity in C9orf72 ALS and/or FTD by RNAi-Based Gene Therapy
Auteur:
Martier, Raygene Liefhebber, Jolanda M. GarcĂa-Osta, Ana Miniarikova, Jana Cuadrado-Tejedor, Mar Espelosin, Maria Ursua, Susana Petry, Harald van Deventer, Sander J. Evers, Melvin M. Konstantinova, Pavlina