RNA-Based Therapy Utilizing Oculopharyngeal Muscular Dystrophy Transcript Knockdown and Replacement
Titel:
RNA-Based Therapy Utilizing Oculopharyngeal Muscular Dystrophy Transcript Knockdown and Replacement
Auteur:
Abu-Baker, Aida Kharma, Nawwaf Perreault, Jonathan Grant, Alanna Shekarabi, Masoud Maios, Claudia Dona, Michele Neri, Christian Dion, Patrick A. Parker, Alex Varin, Luc Rouleau, Guy A.