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Adeno-Associated Virus-Mediated RNAi against Mutant Alleles Attenuates Abnormal Calvarial Phenotypes in an Apert Syndrome Mouse Model |
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Titel: |
Adeno-Associated Virus-Mediated RNAi against Mutant Alleles Attenuates Abnormal Calvarial Phenotypes in an Apert Syndrome Mouse Model |
Auteur: |
Luo, Fengtao Xie, Yangli Wang, Zuqiang Huang, Junlan Tan, Qiaoyan Sun, Xianding Li, Fangfang Li, Can Liu, Mi Zhang, Dali Xu, Meng Su, Nan Ni, Zhenhong Jiang, Wanling Chang, Jinhong Chen, Hangang Chen, Shuai Xu, Xiaoling Deng, Chuxia Wang, Zhugang Du, Xiaolan Chen, Lin |
Verschenen in: |
Molecular therapy - nucleic acids |
Paginering: |
Jaargang 13 () nr. C pagina's 291-302 |
Jaar: |
2018 |
Inhoud: |
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Uitgever: |
The Author(s) |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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