Translating SOD1 Gene Silencing toward the Clinic: A Highly Efficacious, Off-Target-free, and Biomarker-Supported Strategy for fALS
Title:
Translating SOD1 Gene Silencing toward the Clinic: A Highly Efficacious, Off-Target-free, and Biomarker-Supported Strategy for fALS
Author:
Iannitti, Tommaso Scarrott, Joseph M. Likhite, Shibi Coldicott, Ian R.P. Lewis, Katherine E. Heath, Paul R. Higginbottom, Adrian Myszczynska, Monika A. Milo, Marta Hautbergue, Guillaume M. Meyer, Kathrin Kaspar, Brian K. Ferraiuolo, Laura Shaw, Pamela J. Azzouz, Mimoun