Deletion of a Pathogenic Mutation-Containing Exon of COL7A1 Allows Clonal Gene Editing Correction of RDEB Patient Epidermal Stem Cells
Titel:
Deletion of a Pathogenic Mutation-Containing Exon of COL7A1 Allows Clonal Gene Editing Correction of RDEB Patient Epidermal Stem Cells
Auteur:
Mencía, Ángeles Chamorro, Cristina Bonafont, Jose Duarte, Blanca Holguin, Almudena Illera, Nuria Llames, Sara G. Escámez, Maria José Hausser, Ingrid Del Río, Marcela Larcher, Fernando Murillas, Rodolfo