Gene Therapy via Trans-Splicing for LMNA-Related Congenital Muscular Dystrophy
Titel:
Gene Therapy via Trans-Splicing for LMNA-Related Congenital Muscular Dystrophy
Auteur:
Azibani, Feriel Brull, Astrid Arandel, Ludovic Beuvin, Maud Nelson, Isabelle Jollet, Arnaud Ziat, Esma Prudhon, Bernard Benkhelifa-Ziyyat, Sofia Bitoun, Marc Lorain, Stéphanie Bonne, Gisèle Bertrand, Anne T.