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AON-mediated Exon Skipping Restores Ciliation in Fibroblasts Harboring the Common Leber Congenital Amaurosis CEP290 Mutation |
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Title: |
AON-mediated Exon Skipping Restores Ciliation in Fibroblasts Harboring the Common Leber Congenital Amaurosis CEP290 Mutation |
Author: |
Gerard, Xavier Perrault, Isabelle Hanein, Sylvain Silva, Eduardo Bigot, Karine Defoort-Delhemmes, Sabine Rio, Marlèene Munnich, Arnold Scherman, Daniel Kaplan, Josseline Kichler, Antoine Rozet, Jean-Michel |
Appeared in: |
Molecular therapy - nucleic acids |
Paging: |
Volume 1 (2012) nr. C pages 1 p. |
Year: |
2012 |
Contents: |
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Publisher: |
American Society of Gene & Cell Therapy |
Source file: |
Elektronische Wetenschappelijke Tijdschriften |
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