Safe therapeutic gene expression by a lentiviral vector for the gene therapy of autosomal recessive osteopetrosis
Title:
Safe therapeutic gene expression by a lentiviral vector for the gene therapy of autosomal recessive osteopetrosis
Author:
Capo, Valentina Penna, Sara Di Verniere, Martina Draghici, Elena Zonari, Erika Vezzoli, Michela Albertini, Paola Filibian, Marta Forlino, Antonella Sanvito, Francesca Ficara, Francesca Sobacchi, Cristina Gentner, Bernhard Villa, Anna