Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial
Titel:
Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial
Auteur:
Glenthøj, Andreas van Beers, Eduard J Al-Samkari, Hanny Viprakasit, Vip Kuo, Kevin H M Galactéros, Frédéric Chonat, Satheesh Porter, John Zagadailov, Erin Xu, Rengyi Oluyadi, Abdulafeez Hawkins, Peter Gheuens, Sarah Beynon, Vanessa Barcellini, Wilma