Addition of iptacopan, an oral factor B inhibitor, to eculizumab in patients with paroxysmal nocturnal haemoglobinuria and active haemolysis: an open-label, single-arm, phase 2, proof-of-concept trial
Titel:
Addition of iptacopan, an oral factor B inhibitor, to eculizumab in patients with paroxysmal nocturnal haemoglobinuria and active haemolysis: an open-label, single-arm, phase 2, proof-of-concept trial
Auteur:
Risitano, Antonio M Röth, Alexander Soret, Juliette Frieri, Camilla de Fontbrune, Flore Sicre Marano, Luana Alashkar, Ferras Benajiba, Lina Marotta, Serena Rozenberg, Izabela Milojevic, Julie End, Peter Nidamarthy, Prasanna K Junge, Guido Peffault de Latour, Régis