Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial
Titel:
Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial
Auteur:
Coppens, Michiel Pipe, Steven W Miesbach, Wolfgang Astermark, Jan Recht, Michael van der Valk, Paul Ewenstein, Bruce Pinachyan, Karen Galante, Nicholas Le Quellec, Sandra Monahan, Paul E Leebeek, Frank W G