Long-term efficacy and safety of mRNA therapy in two murine models of methylmalonic acidemia
Titel:
Long-term efficacy and safety of mRNA therapy in two murine models of methylmalonic acidemia
Auteur:
An, Ding Frassetto, Andrea Jacquinet, Eric Eybye, Marianne Milano, Joseph DeAntonis, Christine Nguyen, Vi Laureano, Rodrigo Milton, Jaclyn Sabnis, Staci Lukacs, Christine M. Guey, Lin T.