Therapeutic Genome Editing With CRISPR/Cas9 in a Humanized Mouse Model Ameliorates α1-antitrypsin Deficiency Phenotype
Titel:
Therapeutic Genome Editing With CRISPR/Cas9 in a Humanized Mouse Model Ameliorates α1-antitrypsin Deficiency Phenotype
Auteur:
Bjursell, Mikael Porritt, Michelle J. Ericson, Elke Taheri-Ghahfarokhi, Amir Clausen, Maryam Magnusson, Lisa Admyre, Therese Nitsch, Roberto Mayr, Lorenz Aasehaug, Leif Seeliger, Frank Maresca, Marcello Bohlooly-Y, Mohammad Wiseman, John