Lipid nanoparticle delivers phenylalanine ammonia lyase mRNA to the liver leading to catabolism and clearance of phenylalanine in a phenylketonuria mouse model
Titel:
Lipid nanoparticle delivers phenylalanine ammonia lyase mRNA to the liver leading to catabolism and clearance of phenylalanine in a phenylketonuria mouse model
Auteur:
Diaz-Trelles, Ramon Lee, Sharon Kuakini, Kristen Park, Jenny Dukanovic, Adrian Gonzalez, Jose A. Dam, Thanhchau Kim, Jae Heon Vega, Jerel Boyd Sablad, Marciano Karmali, Priya P. Tachikawa, Kiyoshi Chivukula, Padmanabh