Plasma neurofilament light, glial fibrillary acidic protein and lysosphingolipid biomarkers for pharmacodynamics and disease monitoring of GM2 and GM1 gangliosidoses patients
Titel:
Plasma neurofilament light, glial fibrillary acidic protein and lysosphingolipid biomarkers for pharmacodynamics and disease monitoring of GM2 and GM1 gangliosidoses patients
Auteur:
Welford, Richard W.D. Farine, Herve Steiner, Michel Garzotti, Marco Dobrenis, Kostantin Sievers, Claudia Strasser, Daniel S. Amraoui, Yasmina Groenen, Peter M.A. Giugliani, Roberto Mengel, Eugen