Long-term effectiveness of agalsidase alfa enzyme replacement in Fabry disease: A Fabry Outcome Survey analysis
Titel:
Long-term effectiveness of agalsidase alfa enzyme replacement in Fabry disease: A Fabry Outcome Survey analysis
Auteur:
Beck, Michael Hughes, Derralynn Kampmann, Christoph Larroque, Sylvain Mehta, Atul Pintos-Morell, Guillem Ramaswami, Uma West, Michael Wijatyk, Anna Giugliani, Roberto