A non-interventional observational study to identify and validate clinical outcome assessments for adults with phenylketonuria for use in clinical trials
Titel:
A non-interventional observational study to identify and validate clinical outcome assessments for adults with phenylketonuria for use in clinical trials
Auteur:
Burton, Barbara K. Skalicky, Anne Baerwald, Christoph Bilder, Deborah A. Harding, Cary O. Ilan, Aaron B. Jurecki, Elaina Longo, Nicola Madden, David T. Sivri, H. Serap Wilcox, Gisela Thomas, Janet Delaney, Kathleen