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Use of pegvaliase in the management of phenylketonuria: Case series of early experience in US clinics |
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Titel: |
Use of pegvaliase in the management of phenylketonuria: Case series of early experience in US clinics |
Auteur: |
Adams, Darius Andersson, Hans C. Bausell, Heather Crivelly, Kea Eggerding, Caroline Lah, Melissa Lilienstein, Joshua Lindstrom, Kristin McNutt, Markey Ray, Joseph W. Saavedra, Heather Sacharow, Stephanie Starin, Danielle Tiffany-Amaro, Jennifer Thomas, Janet Vucko, Erika Wessenberg, Leah B. Whitehall, Kaleigh |
Verschenen in: |
Molecular genetics and metabolism reports |
Paginering: |
Jaargang 28 () nr. C pagina's p. |
Jaar: |
2021 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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