A phase 1/2 open label nonrandomized clinical trial of intravenous 2-hydroxypropyl-β-cyclodextrin for acute liver disease in infants with Niemann-Pick C1
Titel:
A phase 1/2 open label nonrandomized clinical trial of intravenous 2-hydroxypropyl-β-cyclodextrin for acute liver disease in infants with Niemann-Pick C1
Auteur:
Reynolds, Margaret Linneman, Laura A. Luna, Sofia Warner, Barbara B. Turmelle, Yumirle P. Kulkarni, Sakil S. Jiang, Xuntian Khanna, Geetika Shinawi, Marwan Porter, Forbes D. Ory, Daniel S. Cole, F. Sessions Dickson, Patricia I.