Intravenous delivery of a chemically modified sulfamidase efficiently reduces heparan sulfate storage and brain pathology in mucopolysaccharidosis IIIA mice
Titel:
Intravenous delivery of a chemically modified sulfamidase efficiently reduces heparan sulfate storage and brain pathology in mucopolysaccharidosis IIIA mice
Auteur:
Gustavsson, Susanne Ohlin Sjöström, Elisabet Tjernberg, Agneta Janson, Juliette Westermark, Ulrica Andersson, Tommy Makower, Åsa Arnelöf, Erik Andersson, Gudrun Svartengren, Jan Ekholm, Carina Svensson Gelius, Stefan