Long-term safety and outcomes in hereditary tyrosinaemia type 1 with nitisinone treatment: a 15-year non-interventional, multicentre study
Titel:
Long-term safety and outcomes in hereditary tyrosinaemia type 1 with nitisinone treatment: a 15-year non-interventional, multicentre study
Auteur:
Spiekerkoetter, Ute Couce, Maria L Das, Anibh M de Laet, Corinne Dionisi-Vici, Carlo Lund, Allan M Schiff, Manuel Spada, Marco Sparve, Erik Szamosi, Johan Vara, Roshni Rudebeck, Mattias