Effectiveness and safety of the tri-iodothyronine analogue Triac in children and adults with MCT8 deficiency: an international, single-arm, open-label, phase 2 trial
Titel:
Effectiveness and safety of the tri-iodothyronine analogue Triac in children and adults with MCT8 deficiency: an international, single-arm, open-label, phase 2 trial
Auteur:
Groeneweg, Stefan Peeters, Robin P Moran, Carla Stoupa, Athanasia Auriol, Françoise Tonduti, Davide Dica, Alice Paone, Laura Rozenkova, Klara Malikova, Jana van der Walt, Adri de Coo, Irenaeus F M McGowan, Anne Lyons, Greta Aarsen, Femke K Barca, Diana van Beynum, Ingrid M van der Knoop, Marieke M Jansen, Jurgen Manshande, Martien Lunsing, Roelineke J Nowak, Stan den Uil, Corstiaan A Zillikens, M Carola Visser, Frank E Vrijmoeth, Paul de Wit, Marie Claire Y Wolf, Nicole I Zandstra, Angelique Ambegaonkar, Gautam Singh, Yogen de Rijke, Yolanda B Medici, Marco Bertini, Enrico S Depoorter, Sylvia Lebl, Jan Cappa, Marco De Meirleir, Linda Krude, Heiko Craiu, Dana Zibordi, Federica Oliver Petit, Isabelle Polak, Michel Chatterjee, Krishna Visser, Theo J Visser, W Edward