AAV-mediated gene augmentation therapy of CRB1 patient-derived retinal organoids restores the histological and transcriptional retinal phenotype
Titel:
AAV-mediated gene augmentation therapy of CRB1 patient-derived retinal organoids restores the histological and transcriptional retinal phenotype
Auteur:
Boon, Nanda Lu, Xuefei Andriessen, Charlotte A. Moustakas, Ioannis Buck, Thilo M. Freund, Christian Arendzen, Christiaan H. Böhringer, Stefan Boon, Camiel J.F. Mei, Hailiang Wijnholds, Jan