Human iPSC-based neurodevelopmental models of globoid cell leukodystrophy uncover patient- and cell type-specific disease phenotypes
Titel:
Human iPSC-based neurodevelopmental models of globoid cell leukodystrophy uncover patient- and cell type-specific disease phenotypes
Auteur:
Mangiameli, Elisabeth Cecchele, Anna Morena, Francesco Sanvito, Francesca Matafora, Vittoria Cattaneo, Angela della Volpe, Lucrezia Gnani, Daniela Paulis, Marianna Susani, Lucia Martino, Sabata Di Micco, Raffaella Bachi, Angela Gritti, Angela