Targeted Repair of p47-CGD in iPSCs by CRISPR/Cas9: Functional Correction without Cleavage in the Highly Homologous Pseudogenes
Titel:
Targeted Repair of p47-CGD in iPSCs by CRISPR/Cas9: Functional Correction without Cleavage in the Highly Homologous Pseudogenes
Auteur:
Klatt, Denise Cheng, Erica Philipp, Friederike Selich, Anton Dahlke, Julia Schmidt, Reinhold E. Schott, Juliane W. Büning, Hildegard Hoffmann, Dirk Thrasher, Adrian J. Schambach, Axel