Safety, pharmacokinetics, and pharmacodynamics of lumacaftor and ivacaftor combination therapy in children aged 2–5 years with cystic fibrosis homozygous for F508del-CFTR: an open-label phase 3 study
Titel:
Safety, pharmacokinetics, and pharmacodynamics of lumacaftor and ivacaftor combination therapy in children aged 2–5 years with cystic fibrosis homozygous for F508del-CFTR: an open-label phase 3 study
Auteur:
McNamara, John J McColley, Susanna A Marigowda, Gautham Liu, Fang Tian, Simon Owen, Caroline A Stiles, David Li, Chonghua Waltz, David Wang, Linda T Sawicki, Gregory S