Ivacaftor treatment of cystic fibrosis in children aged 12 to <24 months and with a CFTR gating mutation (ARRIVAL): a phase 3 single-arm study
Titel:
Ivacaftor treatment of cystic fibrosis in children aged 12 to <24 months and with a CFTR gating mutation (ARRIVAL): a phase 3 single-arm study
Auteur:
Rosenfeld, Margaret Wainwright, Claire E Higgins, Mark Wang, Linda T McKee, Charlotte Campbell, Daniel Tian, Simon Schneider, Jennifer Cunningham, Steve Davies, Jane C