Efficacy and safety of lumacaftor and ivacaftor in patients aged 6–11 years with cystic fibrosis homozygous for F508del-CFTR: a randomised, placebo-controlled phase 3 trial
Titel:
Efficacy and safety of lumacaftor and ivacaftor in patients aged 6–11 years with cystic fibrosis homozygous for F508del-CFTR: a randomised, placebo-controlled phase 3 trial
Auteur:
Ratjen, Felix Hug, Christopher Marigowda, Gautham Tian, Simon Huang, Xiaohong Stanojevic, Sanja Milla, Carlos E Robinson, Paul D Waltz, David Davies, Jane C