Safety, pharmacokinetics, and pharmacodynamics of ivacaftor in patients aged 2–5 years with cystic fibrosis and a CFTR gating mutation (KIWI): an open-label, single-arm study
Titel:
Safety, pharmacokinetics, and pharmacodynamics of ivacaftor in patients aged 2–5 years with cystic fibrosis and a CFTR gating mutation (KIWI): an open-label, single-arm study
Auteur:
Davies, Jane C Cunningham, Steve Harris, William T Lapey, Allen Regelmann, Warren E Sawicki, Gregory S Southern, Kevin W Robertson, Sarah Green, Yulia Cooke, Jon Rosenfeld, Margaret