Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial
Titel:
Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial
Auteur:
Kerem, Eitan Konstan, Michael W De Boeck, Kris Accurso, Frank J Sermet-Gaudelus, Isabelle Wilschanski, Michael Elborn, J Stuart Melotti, Paola Bronsveld, Inez Fajac, Isabelle Malfroot, Anne Rosenbluth, Daniel B Walker, Patricia A McColley, Susanna A Knoop, Christiane Quattrucci, Serena Rietschel, Ernst Zeitlin, Pamela L Barth, Jay Elfring, Gary L Welch, Ellen M Branstrom, Arthur Spiegel, Robert J Peltz, Stuart W Ajayi, Temitayo Rowe, Steven M