The expanded French compassionate programme for elexacaftor–tezacaftor–ivacaftor use in people with cystic fibrosis without a F508del CFTR variant: a real-world study
Titel:
The expanded French compassionate programme for elexacaftor–tezacaftor–ivacaftor use in people with cystic fibrosis without a F508del CFTR variant: a real-world study
Auteur:
Burgel, Pierre-Régis Sermet-Gaudelus, Isabelle Girodon, Emmanuelle Durieu, Isabelle Houdouin, Véronique Audousset, Camille Macey, Julie Grenet, Dominique Porzio, Michele Murris-Espin, Marlène Reix, Philippe Baravalle, Mélisande Belleguic, Chantal Mely, Laurent Verhille, Juliette Weiss, Laurence Reynaud-Gaubert, Martine Mittaine, Marie Hamidfar, Rebecca Ramel, Sophie Cosson, Laure Douvry, Benoit Danner-Boucher, Isabelle Foucaud, Pierre Roy, Charlotte Burnet, Espérie Raynal, Caroline Audrezet, Marie-Pierre Da Silva, Jennifer Martin, Clémence