Efficacy and safety of elexacaftor plus tezacaftor plus ivacaftor versus tezacaftor plus ivacaftor in people with cystic fibrosis homozygous for F508del-CFTR: a 24-week, multicentre, randomised, double-blind, active-controlled, phase 3b trial
Titel:
Efficacy and safety of elexacaftor plus tezacaftor plus ivacaftor versus tezacaftor plus ivacaftor in people with cystic fibrosis homozygous for F508del-CFTR: a 24-week, multicentre, randomised, double-blind, active-controlled, phase 3b trial
Auteur:
Sutharsan, Sivagurunathan McKone, Edward F Downey, Damian G Duckers, Jamie MacGregor, Gordon Tullis, Elizabeth Van Braeckel, Eva Wainwright, Claire E Watson, Danie Ahluwalia, Neil Bruinsma, Bote G Harris, Christopher Lam, Anna P Lou, Yiyue Moskowitz, Samuel M Tian, Simon Yuan, Jason Waltz, David Mall, Marcus A