A Single Administration of CRISPR/Cas9 Lipid Nanoparticles Achieves Robust and Persistent In Vivo Genome Editing
Titel:
A Single Administration of CRISPR/Cas9 Lipid Nanoparticles Achieves Robust and Persistent In Vivo Genome Editing
Auteur:
Finn, Jonathan D. Smith, Amy Rhoden Patel, Mihir C. Shaw, Lucinda Youniss, Madeleine R. van Heteren, Jane Dirstine, Tanner Ciullo, Corey Lescarbeau, Reynald Seitzer, Jessica Shah, Ruchi R. Shah, Aalok Ling, Dandan Growe, Jacqueline Pink, Melissa Rohde, Ellen Wood, Kristy M. Salomon, William E. Harrington, William F. Dombrowski, Christian Strapps, Walter R. Chang, Yong Morrissey, David V.