Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia
Titel:
Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia
Auteur:
An, Ding Schneller, Jessica L. Frassetto, Andrea Liang, Shi Zhu, Xuling Park, Ji-Sun Theisen, Matt Hong, Sue-Jean Zhou, Jenny Rajendran, Raj Levy, Becca Howell, Rebecca Besin, Gilles Presnyak, Vladimir Sabnis, Staci Murphy-Benenato, Kerry E. Kumarasinghe, E. Sathyajith Salerno, Timothy Mihai, Cosmin Lukacs, Christine M. Chandler, Randy J. Guey, Lin T. Venditti, Charles P. Martini, Paolo G.V.