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enOsCas12f1-mediated exon skipping for Duchenne muscular dystrophy therapy in humanized mouse model |
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Titel: |
enOsCas12f1-mediated exon skipping for Duchenne muscular dystrophy therapy in humanized mouse model |
Auteur: |
Jin, Ming Lin, Jiajia Zhang, Yu Xiao, Qingquan Kong, Xiangfeng Zhang, Xiumei Shao, Zhurui Wang, Yin Yu, Yuyang Li, Jinjing Chen, Wan-Jin Li, Guoling Yang, Hui Wang, Ning |
Verschenen in: |
Journal of genetics and genomics |
Paginering: |
Jaargang 51 () nr. 2 pagina's 256-259 |
Jaar: |
2024 |
Inhoud: |
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Uitgever: |
Institute of Genetics and Developmental Biology, Chinese Academy of Sciences, and Genetics Society of China |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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